Efficacy and Safety of Dimethyl Fumarate in Friedreich Ataxia: Primary Results From the Phase Two, Randomized, Double-blind, Placebo-controlled DMF-FA-201 Trial (S26.008)

Neurology 2026

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Authors: Francesco Saccà, Martina Gramaglia, Alessio Sarnataro, Angelo Rendina, Giorgia Puorro, Angela Marsili, Chiara Pane, Caterina Giannini, Cosimo Linguetta, Giorgia Esposito, Andrea De Mare, Vittoria Giordano
+3 more Ludovica Aliberti, Antonio Cittadini, Alberto Maria Marra
DOI: 10.1212/wnl.0000000000215751
Cited by: 1

Abstract

Evaluate the efficacy and safety of Dimethyl fumarate (DMF) in patients with Friedreich Ataxia (FA).

Fields of Study & Subjects

Genetic Neurodegenerative Diseases Amyotrophic Lateral Sclerosis Research Glycogen Storage Diseases and Myoclonus

Publication details

Journal / source
Neurology
Publisher
Ovid Technologies (Wolters Kluwer Health)
Volume
106
Issue
11_Supplement_1
Publication date
9 June 2026
Language
EN