Publication Gap in Rare Disease Clinical Trials: A Retrospective Cohort Study of Trials Registered in ClinicalTrials.gov (2015-2021)
Abstract
This study examines the publication rate of completed rare disease clinical trials registered in ClinicalTrials.gov (2015-2021) and identifies factors associated with publication. We aim to quantify the knowledge gap created by unpublished trials and its impact on clinical practice.
Fields of Study & Subjects
Meta-analysis and systematic reviews
Pharmaceutical industry and healthcare
Academic Publishing and Open Access
Publication details
- Publication date
- 1 January 2026
- Document type
- Preprint