Reproducible Computational Framework for Precision RNA Targeting in Myotonic Dystrophy Type 1: Balancing ASO Specificity and Cas13 Potency at the DMPK Locus

Research Square 2026 Preprint Open access

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Authors: Seyed Mohammad Javad Hashemi
DOI: 10.21203/rs.3.rs-8456938/v1
Cited by: 0
References: 54

Fields of Study & Subjects

Genetic Neurodegenerative Diseases RNA Research and Splicing Genomics and Rare Diseases

Publication details

Journal / source
Research Square
Publication date
6 January 2026
Document type
Preprint