AAV-Mediated HPD Gene Silencing Rescues Lethal Liver Injury in a FAH Knockout Rabbit Model of Hereditary Tyrosinemia Type I

SSRN Electronic Journal 2026 Preprint Open access

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Authors: Hailong Su, Chula Sa, Guiling Li, Tianping Liu, Gang Wang, Bangzhu Chen, GU Wei-wang
DOI: 10.2139/ssrn.6087155
Cited by: 0

Fields of Study & Subjects

Metabolism and Genetic Disorders Virus-based gene therapy research RNA Interference and Gene Delivery

Publication details

Journal / source
SSRN Electronic Journal
Publication date
1 January 2026
Document type
Preprint