MassIVE MSV000101131 - MSI of systemic AAV9 gene therapy in Niemann-Pick disease, type C1 mice

Read full text
Authors: Stephanie M. Cologna
Cited by: 0

Fields of Study & Subjects

Lysosomal Storage Disorders Research Virus-based gene therapy research RNA Interference and Gene Delivery

Publication details

Journal / source
UC San Diego
Publication date
1 January 2026
Language
EN
Document type
Dataset