MassIVE MSV000101131 - MSI of systemic AAV9 gene therapy in Niemann-Pick disease, type C1 mice
Fields of Study & Subjects
Lysosomal Storage Disorders Research
Virus-based gene therapy research
RNA Interference and Gene Delivery
Publication details
- Journal / source
- UC San Diego
- Publication date
- 1 January 2026
- Language
- EN
- Document type
- Dataset