Terapia com CRISPR-CAS9 na Beta-Talassemia: Mecanismos de Correção Gênica e Potencial Terapêutico

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Authors: Elis Maria Tiburcio Lins de Azevedo, Rodrigo Rafael Domingos Quaresma De Andrade, Clarissa Dantas Valdivino, Beatriz Vitórya Florêncio Gualberto, Maria Júlia Alves Magalhães, Ana Lara Alves Costa Pereira, Maria Beatriz Mendonça Aguiar Oliveira da Silva, Bárbara Beatriz Soares da Silva, Tamara de Carli da Costa Lima
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Fields of Study & Subjects

Hemoglobinopathies and Related Disorders CRISPR and Genetic Engineering Virus-based gene therapy research

Publication details

Pages
61–63
Publication date
20 January 2026