Consistency Assessment of Regional Treatment Effect for Multi-Regional Clinical Trials in the Presence of Covariate Shift

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Authors: Kunhai Qing, Xinru Ren, Jin Xu, Menggang Yu
Cited by: 0

Abstract

Multi-Regional Clinical Trials (MRCTs) play a central role in the development of new therapies by enabling the simultaneous evaluation of drug efficacy and safety across diverse global populations. Assessing the consistency of treatment effects across regions is a fundamental aspect of MRCTs. Existing methods typically focus on region-specific marginal treatment effects. However, when treatment effect heterogeneity arises due to effect-modifying baseline covariates, distributional differences in these covariates can lead to erroneous conclusions. In this paper, we explicitly account for this phenomenon in the consistency assessment by considering the conditional average treatment effect. We propose a two-step assessment strategy that complements existing methods and mitigates the impact of treatment effect heterogeneity. Results from numerical studies demonstrate the effectiveness of the proposed approach.

Fields of Study & Subjects

Statistical Methods in Clinical Trials Advanced Causal Inference Techniques Statistical Methods and Bayesian Inference

Publication details

Journal / source
arXiv (Cornell University)
Publication date
7 February 2026
Language
EN
Document type
Preprint