GoldbergNeuroLab/Nelson_Hill_Simon_et_al_2026: In vivo adenine base editing rescues Dravet Syndrome in mice v2
Fields of Study & Subjects
Epilepsy research and treatment
CRISPR and Genetic Engineering
RNA regulation and disease
Publication details
- Journal / source
- Zenodo (CERN European Organization for Nuclear Research)
- Publication date
- 12 January 2026