Additional file 1 of AAV9 gene therapy optimization for SMARD1/CMT2S: safety and long-term efficacy comparison of two vectors in a SMARD1 preclinical model

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Authors: Elisa Pagliari, Alessia Anastasia, Floriana Bellandi, Manuela Garbellini, Jessica Ongaro, Michela Maria Taiana, Giacomo P. Comi, Linda K. Ottoboni, Julieth A. Sierra-Delgado, Shibi B. Likhite, Kathrin Meyer, Monica Nizzardo
+1 more Stefania P. Corti
DOI: 10.6084/m9.figshare.30997126
Cited by: 0

Fields of Study & Subjects

Hereditary Neurological Disorders Neurogenetic and Muscular Disorders Research Genomics and Rare Diseases

Publication details

Journal / source
Figshare
Publication date
1 January 2026