Additional file 1 of Clinical outcomes of exclusive enzyme therapy (laronidase) in a cohort of patients with mucopolysaccharidosis type I

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Authors: Nathalie Guffon, Magali Pettazzoni, Nicolas Pangaud, Nathalie Reynes, Eliane Le Peillet Feuillet, P. Journeau, Alain Fouilhoux

DOI: 10.6084/m9.figshare.31054416

Cited by: 0

Fields of Study & Subjects

Lysosomal Storage Disorders Research Glycogen Storage Diseases and Myoclonus Proteoglycans and glycosaminoglycans research