Additional file 1 of Economic evaluations of disease-modifying therapies for spinal muscular atrophy: a systematic literature review

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Authors: Mehdi Yousefi, Amin Mehrabian, Anna Brown, Furqan Butt, J Donoghue, Janette Parr, Mubarak Patel, Amy Grove, Jo Parsons, Peter Auguste
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Fields of Study & Subjects

Neurogenetic and Muscular Disorders Research Health Systems Economic Evaluations Quality of Life Amyotrophic Lateral Sclerosis Research

Publication details

Journal / source
Figshare
Publication date
1 January 2026