Sirolimus plus roxadustat in acquired pure red cell aplasia: a single-arm, open-label, multicenter trial
Abstract
This dataset contains the results of a clinical trial in which sirolimus was combined with roxadustat to treat patients with pure red cell aplasia. Of the 82 enrolled patients, 7 withdrew for various reasons, and 3 discontinued treatment due to adverse events. The file includes baseline data for the 72 patients who were included in the efficacy analysis: sex, age, disease type, secondary factor, baseline hemoglobin, reticulocyte count, ferritin, and erythropoietin. It also evaluates efficacy at 3 months and 6 months and reports treatment-related adverse events during the treatment.VariablesHB:hemoglobinRet:reticulocyte countsFer:serum ferritinEPO:erythropoietinCR:complete response;PR:partial response;NR:no response;OR:overall responseTRAE: Treatment-related adverse eventsFatigue score: using Functional Assessment of Chronic Illness Therapy-Fatigue ScaleSF-36 survey scores: includes eight subscales with scores ranging 0–100. PF, physical functioning; RP, role physical; BP, bodily pain; GH, general health; VT, vitality; SF, social functioning; RE, role–emotional; MH, mental health.
Fields of Study & Subjects
Erythropoietin and Anemia Treatment
Blood disorders and treatments
Hematological disorders and diagnostics
Publication details
- Journal / source
- Figshare
- Publication date
- 1 January 2026
- Document type
- Dataset