Additional file 1 of Impact of glycerol phenylbutyrate on biochemistry and outcomes in paediatric patients with urea cycle disorders: a multicentre case series from Saudi Arabia

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Authors: Rawan Hejazi, Thamer H. Alghamdi, Rihab M. Salih, Yousra Naeim, Hamad Althiyab, Talal S.A. Alanzi, Sarar Mohamed, Majid Alfadhel, Ruqaiah Altassan, Zuhair N. Al‐Hassnan, Moeenaldeen Dia Alsayed
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Fields of Study & Subjects

Metabolism and Genetic Disorders Amino Acid Enzymes and Metabolism Neonatal Health and Biochemistry

Publication details

Journal / source
Figshare
Publication date
1 January 2026
Language
EN