A Phase II Basket Trial of Vosoritide in Children with RASopathies, ACAN and NPR2 Deficiency - Supplementary Materials
Abstract
These are supplementary data, a research protocol and statistical analysis plan that accompany a manuscript.
Fields of Study & Subjects
Connective tissue disorders research
Genomics and Rare Diseases
Protein Tyrosine Phosphatases
Publication details
- Journal / source
- Figshare
- Publication date
- 11 March 2026
- Language
- EN