Targeting Pathogenic Genes in Spinocerebellar Ataxia Using Novel Antisense Oligonucleotides
Fields of Study & Subjects
Genetic Neurodegenerative Diseases
Amyotrophic Lateral Sclerosis Research
RNA Interference and Gene Delivery
Publication details
- Journal / source
- Therapeutic Innovation Australia
- Publication date
- 17 February 2026
- Language
- EN