Real-world use and cost-effectiveness of orphan drugs for Spinal muscular atrophy: protocol of a systematic literature review

OSF Preprints (OSF Preprints) 2026 Preprint

Authors: Neli Boseva-Stoyanova, Alexandra Savova, Maria Kamusheva
Cited by: 0

Fields of Study & Subjects

Neurogenetic and Muscular Disorders Research Health Systems Economic Evaluations Quality of Life Pharmaceutical Economics and Policy

Publication details

Journal / source
OSF Preprints (OSF Preprints)
Publication date
13 February 2026
Language
EN
Document type
Preprint